video: DOK7 therapy benefits mouse models of DOK7 congenital myasthenic syndrome (Dok-7 KI mice) and autosomal dominant\r\nEmery-Dreifuss muscular dystrophy (Lmna KO mice). This material relates to a paper that appeared in the 19 Sept., issue of Science, published by AAAS. The paper, by S. Arimura at The University of Tokyo in Tokyo, Japan, and colleagues was titled, "DOK7 gene therapy benefits mouse models of diseases characterized by defects in the neuromuscular junction." view more
Credit: [Credit: Sumimasa Arimura and Yuji Yamanashi]