News by Subject Medicine & Health

Exploitation in 'crowdsourced' research, oversight of right-to-try access to experimental drugs, and more.

American and British teams published yesterday in Nature Medicine the conclusive results of a gene therapy trial conducted in the United States and Great Britain in 9 patients with X-linked Chronic Septic Granulomatosis (X-CGD), a rare and severe immune dysfunction. Genethon, which contributed to the research that led to these trials and sponsored initial clinical studies, is pleased with these results.

Research by a University of Georgia psychologist shows that targeting one particular symptom of schizophrenia has a positive effect on other symptoms.

A new study shows artificial intelligence (AI) analysis of blood samples can predict and explain disease progression, which could one day help doctors choose more appropriate and effective treatments for patients.

A groundbreaking tumor-highlighting technology -- OTL38 -- enhances the visualization of lung cancer tissue, providing surgeons with a significantly better chance of finding and removing more cancer than previously possible.

A new human Bone Marrow Chip that more closely recapitulates drug- and radiation-induced responses observed in patients (e.g., as a result of cancer treatments), and was used to uncover a previously unknown abnormality in the bone marrow of patients with a rare genetic disorder, and sets the stage for better toxicology studies and personalized medicine.

An MRI study investigating the influence of changes in the neuroanatomy of trigeminal neuralgia found that both trigeminal nerve and brain structures such as the hippocampus can predict the surgical treatment outcome. Greater trigeminal nerve and hippocampus volumes were more associated with non-responders patients.

A new study analyzes 30 years of patient data and details the clinical course of 184 individuals with genetically diverse forms of Maple Syrup Urine Disease (MSUD), which is among the most volatile and dangerous inherited metabolic disorders.